List of gene therapies

This article contains a list of commercially available gene therapies.

Gene therapies

 * Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency (no longer commercially available)
 * Axicabtagene ciloleucel (Yescarta): treatment for large B-cell lymphoma
 * Beremagene geperpavec (Vyjuvek): treatment of wounds.
 * Betibeglogene autotemcel (Zynteglo): treatment for beta thalassemia
 * Brexucabtagene autoleucel (Tecartus): treatment for mantle cell lymphoma and acute lymphoblastic leukemia
 * Cambiogenplasmid (Neovasculgen): treatment for vascular endothelial growth factor peripheral artery disease
 * Ciltacabtagene autoleucel (Carvykti): treatment for multiple myeloma
 * Delandistrogene moxeparvovec (Elevidys): treatment for Duchenne muscular dystrophy
 * Elivaldogene autotemcel (Skysona): treatment for cerebral adrenoleukodystrophy
 * Etranacogene dezaparvovec (Hemgenix): AAV-based treatment for hemophilia B
 * Exagamglogene autotemcel (Casgevy): treatment for sickle cell disease.
 * Gendicine: treatment for head and neck squamous cell carcinoma
 * Idecabtagene vicleucel (Abecma): treatment for multiple myeloma
 * Lovotibeglogene autotemcel (Lyfgenia): treatment for sickle cell disease.
 * Nadofaragene firadenovec (Adstiladrin): treatment for bladder cancer
 * Onasemnogene abeparvovec (Zolgensma): AAV-based treatment for spinal muscular atrophy
 * Strimvelis: treatment for adenosine deaminase deficiency (ADA-SCID)
 * Talimogene laherparepvec (Imlygic): treatment for melanoma in patients who have recurring skin lesions
 * Tisagenlecleucel (Kymriah): treatment for B cell lymphoblastic leukemia
 * Valoctocogene roxaparvovec (Roctavian): treatment for hemophilia A
 * Voretigene neparvovec (Luxturna): AAV-based treatment for Leber congenital amaurosis