User:Mr. Ibrahem/Migalastat

Migalastat, sold under the brand name Galafold, is a medication used to treat Fabry disease. It is only used for certain types of the disease. It is taken by mouth. It is used in those who are at least 12 years old.

Common side effects include headache, runny nose, fever, nausea, and urinary tract infection. Safety in pregnancy is unclear. It works by attaching to certain forms of the enzyme alpha-galactosidase A and stabilizing it.

Migalastat was approved for medical use in Europe in 2016 and the United States in 2018. In the United States it costs about 315,000 USD per year as of 2020. In the United Kingdom this amount costs the NHS about £121,000.